FDA lifts clinical hold on studies of LentiGlobin in sickle cell disease and beta-thalassemia June 8, 2021 No Comments
SPK-10000, a liver-targeted gene therapy for the treatment of hereditary angioedema June 1, 2021 No Comments
Phase I trial explores use of BIVV-001 in adults with type 2N and 3 von Willebrand disease May 31, 2021 No Comments
Phase I data on SLN-124 support ongoing evaluation in patients with thalassemia and MDS May 19, 2021 No Comments
FDA approves Ferriprox to treat transfusional iron overload due to sickle cell disease May 3, 2021 No Comments
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