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Home » Mass spec(ulation) blots DMD gene therapy space as PPMD data come soon
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Mass spec(ulation) blots DMD gene therapy space as PPMD data come soon

June 19, 2019
By Randy Osborne
Last week at the Goldman Sachs Healthcare Conference in Rancho Palos Verdes, Calif., Sarepta Therapeutics Inc. CEO Douglas Ingram noted that "more than a kid a day dies" from Duchenne muscular dystrophy (DMD) in the U.S., adding that officials at his Cambridge, Mass.-based firm "feel an enormous obligation to move heaven and earth to get this [gene] therapy to the community if it's possible" and quickly.
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