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Home » Keeping the doctor away: Orchard gene therapy bid promising in MPS-I, more
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Keeping the doctor away: Orchard gene therapy bid promising in MPS-I, more

Sep. 10, 2019
By Randy Osborne
As Wall Street ponders how pricing and reimbursement for gene therapies might shake out, companies in the field march intrepidly on, among them Orchard Therapeutics Inc., which early this month rolled out heartening results from an ongoing proof-of-concept trial evaluating the safety and efficacy of OTL-203 for mucopolysaccharidosis type I (MPS-I), a space that's heating up.
BioWorld Clinical Endocrine/metabolic Gene therapy

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