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Breaking News: Trump administration impacts continue to roil the life sciences sectorSee today's BioWorld Science
Home » Neurogene's gene therapy NGN-401 cleared to enter clinic for Rett syndrome
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Neurology/Psychiatric

Neurogene's gene therapy NGN-401 cleared to enter clinic for Rett syndrome

Jan. 24, 2023
Neurogene Inc. has received FDA clearance of its IND application for NGN-401 for the treatment of Rett syndrome. The company plans to initiate a phase I/II trial in female pediatric patients with Rett syndrome this year.
BioWorld Science Neurology/psychiatric Gene therapy FDA IND

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