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Home » Ethical considerations open FDA’s Rare Disease Day
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Ethical considerations open FDA’s Rare Disease Day

Feb. 27, 2023
By Lee Landenberger
The U.S. FDA marked the 40th anniversary of the Orphan Drug Act with Rare Disease Day 2023 as Robert Califf, the agency’s commissioner of food and drugs, opened the day by expressing his wonder and accompanying concern regarding gene editing and gene therapy.
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