Dtx Pharma’s siRNA therapeutic Dtx-1252 awarded US orphan drug designation for CMT1A
June 8, 2023
Dtx Pharma Inc.’s Dtx-1252, an investigational small interfering RNA (siRNA) therapeutic, has been awarded U.S. orphan drug designation for the treatment of Charcot-Marie-Tooth disease type 1A (CMT1A).