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Home » Next-generation genome editing tools surpass CRISPR milestone
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Next-generation genome editing tools surpass CRISPR milestone

Jan. 4, 2024
By Anette Breindl and Mar de Miguel
Modifying a patient’s DNA is no longer just for science fiction novels. The CRISPR gene editing technique developed by Jennifer Doudna and Emmanuelle Charpentier only took 10 years to reach the market as Casgevy (exagamglogene autotemcel/exa-cel, Vertex Pharmaceuticals Inc.), treating congenital pathologies such as β-thalassemia and severe sickle cell disease. But science does not stop.
BioWorld Bioengineering Drug design, drug delivery and technologies Gene therapy Genetic/congenital

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