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Home » Medipal and JCR move JR-446 toward clinic in Japan for mucopolysaccharidosis type IIIB
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Endocrine/metabolic

Medipal and JCR move JR-446 toward clinic in Japan for mucopolysaccharidosis type IIIB

July 2, 2024
Medipal Holdings Corp. and JCR Pharmaceuticals Co. Ltd. have announced the completion of the clinical trial notification review by Japan’s Pharmaceuticals and Medical Devices Agency (PMDA) for a phase I/II study of JR-446 for the treatment of mucopolysaccharidosis type IIIB (MPS IIIB; Sanfilippo syndrome type B).
BioWorld Science Regulatory Endocrine/metabolic PMDA

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