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» Houston, a problem: Rocket death in Danon stalls phase II program
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Houston, a problem: Rocket death in Danon stalls phase II program
May 27, 2025
By
Randy Osborne
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Rocket Pharmaceuticals Inc. CEO Gaurav Shah said his firm is investigating how its gene therapy for Danon disease may have created an “unexpected and paradoxical” effect that led to problems for a phase II patient who ultimately died.
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