Reblozyl approved in Europe for transfusion-dependent anemia in MDS or beta-thalassemia June 29, 2020 No Comments
Primary endpoint met in phase II study of garadacimab as preventive treatment in HAE June 9, 2020 No Comments
FDA clears Expression Therapeutics' IND for phase I trial of gene therapy for hemophilia A May 28, 2020 No Comments
In vivo data support human trials of CRISPR/Cas9-mediated homology-directed repair treatment for SCD May 28, 2020 No Comments