FDA grants rare pediatric disease designation to sevuparin for children with sickle cell disease April 19, 2018
First subject dosed in phase I/IIa trial of SYNB-1618 for the treatment of phenylketonuria April 19, 2018
FDA grants orphan drug designation to KL-1333 for inherited mitochondrial respiratory chain diseases April 18, 2018
First-in-human study of ATX-GD-59 in patients with Graves' disease meets primary endpoint April 17, 2018
Kalytera terminates preclinical programs for synthetic endocannabinoid compounds in bone disease April 17, 2018