FDA lifts clinical hold on studies of LentiGlobin in sickle cell disease and beta-thalassemia June 8, 2021 No Comments
SPK-10000, a liver-targeted gene therapy for the treatment of hereditary angioedema June 1, 2021 No Comments
Phase I trial explores use of BIVV-001 in adults with type 2N and 3 von Willebrand disease May 31, 2021 No Comments
Phase I data on SLN-124 support ongoing evaluation in patients with thalassemia and MDS May 19, 2021 No Comments