AAV-mediated liver delivery of secretable GAA improves long-term survival in Pompe disease mice Dec. 28, 2017
Summit acquires Discuva and obtains innovative antibiotic discovery and development platform Dec. 27, 2017
Agios submits NDA for ivosidenib to treat relapsed/refractory AML with an IDH1 mutation Dec. 27, 2017
FDA grants fast track designation to cannabidiol oral solution for Prader-Willi syndrome Dec. 27, 2017
Soliris approved in Japan for the treatment of patients with generalized myasthenia gravis Dec. 27, 2017