DISC-0974 decreases hepcidin and increases transferrin saturation in inflammation models Dec. 28, 2020 No Comments
PKLR activator mitapivat shows promising preclinical data in murine hereditary spherocytosis Dec. 23, 2020 No Comments
CSL pact intact as Uniqure works to FIX hemophilia B gene therapy stall Dec. 22, 2020 By Randy Osborne No Comments Amsterdam-based Uniqure NV’s regulatory hitch with its highly regarded hemophilia B program had analysts questioning during a conference call what the development might mean for the company’s deal with CSL Ltd.Read More
Phase III HOPE-B study of etranacogene dezaparvovec meets first coprimary endpoint Dec. 22, 2020 No Comments
Singapore HSA approves CANbridge's IND for CAN-106 for complement dysregulation diseases Dec. 22, 2020 No Comments